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12-01-2024

Minimal clinically important difference in the World Health Organization Quality of Life Brief (WHOQOL-BREF) for adults with neurofibromatosis

Auteurs: Malvina O. Pietrzykowski, Ana-Maria Vranceanu, Eric A. Macklin, Ryan A. Mace

Gepubliceerd in: Quality of Life Research | Uitgave 5/2024

Abstract

Purpose

This study aimed to estimate minimal clinically important difference (MCID) values for the World Health Organization Quality of Life Brief version (WHOQOL-BREF) among adults with neurofibromatosis (NF). An MCID is needed to demonstrate clinical meaningfulness of interventions for NF.

Methods

We estimated MCID for the WHOQOL-BREF: the quality of life (QoL) measure recommended by the Response Evaluation in Neurofibromatosis and Schwannomatosis International Collaboration. We used data from 228 clinical trial participants with NF type 1, NF type 2-related schwannomatosis, or schwannomatosis (SCHWN) who completed 10 weeks of a virtual group mind–body program targeting resiliency or a time- and attention-matched control. Following established guidelines, we estimated MCIDs using both anchor-based and distribution-based methods for physical, psychological, social relationships, and environmental domains of the WHOQOL-BREF.

Results

MCID results varied across method and QoL domain. Three anchor-based methods, average change (AC), change difference (CD), and regression (REG), yielded the most consistent and comparable MCID across QoL domains. Based on these methods, we recommend ranges for each QoL domain: Physical QoL (3.9–7.3), Psychological QoL (4.7–8.1), Social QoL (2.6–5.9), and Environmental QoL (4.1–6.6).

Conclusion

Establishing a rigorous MCID for QoL in NF is a critical step toward evaluating meaningful change in response to psychosocial interventions.

vorige artikel Anchor-based minimal important difference values are often sensitive to the distribution of the change score

volgende artikel Power analyses for measurement model misspecification and response shift detection with structural equation modeling

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Titel: Minimal clinically important difference in the World Health Organization Quality of Life Brief (WHOQOL-BREF) for adults with neurofibromatosis
Auteurs: Malvina O. Pietrzykowski
Ana-Maria Vranceanu
Eric A. Macklin
Ryan A. Mace
Publicatiedatum: 12-01-2024
Uitgeverij: Springer International Publishing
Gepubliceerd in: Quality of Life Research / Uitgave 5/2024
Print ISSN: 0962-9343
Elektronisch ISSN: 1573-2649
DOI: https://doi.org/10.1007/s11136-023-03596-7

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Minimal clinically important difference in the World Health Organization Quality of Life Brief (WHOQOL-BREF) for adults with neurofibromatosis

Abstract

Purpose

Methods

Results

Conclusion

Andere artikelen Uitgave 5/2024

Sexual health in Belgian cervical cancer survivors: an exploratory qualitative study

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Evaluation of the internet-based intervention “Selfapy” in participants with unipolar depression and the impact on quality of life: a randomized, parallel group study

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Abstract

Purpose

Methods

Results

Conclusion

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Sexual health in Belgian cervical cancer survivors: an exploratory qualitative study

Health-related quality of life and associated risk factors in patients with Multiple Osteochondromas: a cross-sectional study

Scoring the EQ-HWB-S: can we do it without value sets? A non-parametric item response theory analysis

Anchor-based minimal important difference values are often sensitive to the distribution of the change score

Health-related quality of life in patients with extremity bone sarcoma after surgical treatment: a systematic review

Evaluation of the internet-based intervention “Selfapy” in participants with unipolar depression and the impact on quality of life: a randomized, parallel group study